Nonviral delivery of a base editor enables personalized correction of hemophilia B nonsense variants in a mouse model
Authors: Uchina Hiya-Kawaguchi, Yuji Kashiwakura, Nemekhbayar Baatartsogt et al.
Publication: Journal of Thrombosis and Haemostasis
Published: Sep 1, 2026
Source: Crossref
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